Our focus is urgent because the need is great. We develop new therapies with an urgent and unwavering focus for patients living with rare genetic skin diseases.
>1000
References
605 diseases according to https://rarediseases.info.nih.gov/diseases/diseases-by-category/22/skin-diseases but these are genetic skin diseases so that is likely low. In fact this recent source (from a well-known investigator in the field) claims over 1000: https://ojrd.biomedcentral.com/articles/10.1186/s13023-018-0944-x.
Rare skin diseases identified
0.6%<
FDA approvals for rare skin conditions
transparency
We actively involve patients in our R&D process in order to develop drugs with meaningful data.
pipeline
Our pioneering pipeline harnesses innovation from every facet of drug development, from mechanism of action, to route of administration, to novel targeting technology.
approach
We are bringing together the worlds of orphan drug and dermatology drug development.