Our focus is urgent because the need is great. We develop new therapies with an urgent and unwavering focus for patients living with rare genetic skin diseases.
605 diseases according to https://rarediseases.info.nih.gov/diseases/diseases-by-category/22/skin-diseases but these are genetic skin diseases so that is likely low. In fact this recent source (from a well-known investigator in the field) claims over 1000: https://ojrd.biomedcentral.com/articles/10.1186/s13023-018-0944-x.
Rare skin diseases identified
FDA approvals for rare skin conditions
We actively involve patients in our R&D process in order to develop drugs with meaningful data.
Our pioneering pipeline harnesses innovation from every facet of drug development, from mechanism of action, to route of administration, to novel targeting technology.
We are bringing together the worlds of orphan drug and dermatology drug development.